Gene therapy

Gene therapy for haemophiliaGene therapy for haemophilia

Information for people with haemophilia about gene therapy and how it works in haemophilia. This booklet explains the types of gene therapy that are being trialled in haemophilia at present, who can have gene therapy, what the process involves for a person having gene therapy, and how effective it is, safety and side-effects. It uses easy to read language and diagrams to explain how gene therapy for haemophilia works in the body. It also covers FAQs from the community.

October 2019 edition

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Date last reviewed: 23 October 2019